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Morquio Syndrome Treatment Market

Global Morquio Syndrome Treatment Market Share, Forecast: By Disease Type: Morquio A, Morquio B; By Treatment: Enzyme Replacement Therapy, Others; By Distribution Channels: Hospital Pharmacies, Retail Pharmacies, Online; Regional Analysis; Competitive Landscape; Key Trends and Developments in the Market; 2024-2032

Global Morquio Syndrome Treatment Market Outlook

The global morquio syndrome treatment market size is expected to grow at a CAGR of 5.70% between 2024 and 2032. The development is aided by the rising prevalence of inherited diseases and increasing demand for specialised medication in treatment.

 

Global Morquio Syndrome Treatment Market Trends

Morquio syndrome is a rare genetic syndrome that is inherited during birth and affects a child’s bones, spine, organs, which create deformities and affect his/her physical capabilities. It is also known as MPS IV. The symptom of this disease is usually not visible at birth, they come to notice between the ages of 1 and 3. The most problematic part of this disease is that it is a progressive disease which means it gets worse as the child grows older.

 

This disease is a part of a group of diseases which are known as mucopolysaccharidosis (MPS).

 

  • The rising prevalence of congenital diseases is a major factor behind the development of the market. Due to the rising cases, healthcare centres are continuously implementing advanced treatment methods that can improve the patient’s experience.
  • Key players in the market are increasingly engaging in mergers and collaborative partnerships with an aim to innovate and develop specialized treatment procedures. This factor can significantly help in market expansion, especially with governments investing in development ventures to meet the increasing demand for specialized medications.
  • The growing number of products approved by regulatory organisations can significantly help in market growth. This also provides market players with positive opportunities to develop innovative medicines, which can further propel market development.

 

Global Morquio Treatment Market Analysis

Based on disease type, the market can be segmented into morquio A and morquio B. Based on the treatment, it can be bifurcated into enzyme replacement therapy and others. Based on distribution channels, the market can be segmented into hospital pharmacies, retail pharmacies, and online. The regional markets for morquio syndrome treatment can be divided into North America, Europe, the Asia Pacific, Latin America, the Middle East and Africa.

 

The comprehensive EMR report provides an in-depth assessment of the market based on Porter's five forces model along with giving a SWOT analysis. The report gives a detailed analysis of the following key players in the global morquio syndrome treatment market, covering their competitive landscape and the latest developments like mergers, acquisitions, investments and expansion plans.

 

  • BioMarin Pharmaceutical Inc.
  • JCR Pharmaceuticals Co., Ltd.
  • Sanofi
  • Sangamo Therapeutics
  • Alexion Pharmaceuticals Inc.
  • Others

 

Disease Types in the Morquio Syndrome Treatment Market

The market for morquio syndrome treatment can be categorised by disease type into Morquio A and Morquio B.

 

Morquio A, which is also known as MPS IVA, is an autosomal recessive genetic disorder that affects a person due to the deficiency of GALNS enzyme, which occurs because of a mutation in the GALNS gene. People affected by the glycosaminoglycan diseases have trouble producing enough enzymes that are required to break down the sugar chains into simple molecules.

 

Morquio B, also called MPS IVB, is a genetic disorder that occurs due to the deficiency of the beta-galactosidase enzyme. This occurs due to a mutation in the GLB1 gene.

 

Major Regional Markets for Morquio Syndrome Treatment

The market for Morquio syndrome treatment can be geographically divided into various regions including North America, Europe, the Asia Pacific, Latin America, the Middle East and Africa.

 

Among these regions, North America is expected to be the major region for the market. The development of the market in this region can be attributed to the rising prevalence of diseases, the development of advanced treatment methods and the rising demand for such methods, and the presence of developed healthcare infrastructure.

 

morquio syndrome treatment market by region

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Competitive Landscape

BioMarin Pharmaceutical Inc. is one of the leading biotechnology companies with their core business and research focus on enzyme replacement therapies. The company was established in 1997 and the headquarter is located in California, United States. Their product portfolio consists of treatment solutions and injections related to rare genetic disorders.

 

JCR Pharmaceuticals Co., Ltd. is a Japanese-based pharmaceutical company operating with an aim to improve people’s healthcare with pharmaceutical products. The company was founded in 1975 and they have developed its list of products to consist of growth hormones, lysosomal disease treatment products, regenerative medical products, and renal anaemia.

 

Sanofi is a French-based multinational company, considered a global healthcare leader in the development of pharmaceutical products specialised according to the needs of people. The company specialises in vaccines, rare disease treatment products, neurology, immunology, oncology, cardiovascular diseases, and consumer healthcare. The company was formed in the year of 1973 and later it got merged with Synthélabo in 1999.

 

Other market players include Sangamo Therapeutics and Alexion Pharmaceuticals Inc., among others.

 

Key Highlights of the Report

REPORT FEATURES DETAILS
Base Year 2023
Historical Period 2017-2023
Forecast Period 2024-2032
Scope of the Report

Historical and Forecast Trends, Industry Drivers and Constraints, Historical and Forecast Market Analysis by Segment:

  • Disease Type
  • Treatment
  • Distribution Channels
  • Region
Breakup by Disease Type
  • Morquio A
  • Morquio B
Breakup by Treatment
  • Enzyme Replacement Therapy
  • Others
Breakup by Distribution Channels
  • Hospital Pharmacies
  • Retail Pharmacies
  • Online
Breakup by Region
  • North America
    • United States of America 
    • Canada
  • Europe
    • United Kingdom
    • Germany
    • France
    • Italy
    • Others
  • Asia Pacific
    • China
    • Japan
    • India
    • ASEAN
    • Australia
    • Others
  • Latin America
    • Brazil
    • Argentina
    • Mexico
    • Others
  • Middle East and Africa
    • Saudi Arabia
    • United Arab Emirates
    • Nigeria
    • South Africa
    • Others
Market Dynamics
  • SWOT Analysis
  • Porter's Five Forces Analysis
  • Key Indicators for Demand
  • Key Indicators for Price
Competitive Landscape
  • Market Structure
  • Company Profiles
    • Company Overview
    • Product Portfolio
    • Demographic Reach and Achievements
    • Certifications
Companies Covered
  • BioMarin Pharmaceutical Inc.
  • JCR Pharmaceuticals Co., Ltd.
  • Sanofi
  • Sangamo Therapeutics
  • Alexion Pharmaceuticals Inc.
  • Others

 

*At Expert Market Research, we strive to always give you current and accurate information. The numbers depicted in the description are indicative and may differ from the actual numbers in the final EMR report.

1    Preface 
2    Report Coverage – Key Segmentation and Scope
3    Report Description

    3.1    Market Definition and Outlook
    3.2    Properties and Applications
    3.3    Market Analysis
    3.4    Key Players
4    Key Assumptions   
5    Executive Summary

    5.1    Overview
    5.2    Key Drivers
    5.3    Key Developments  
    5.4    Competitive Structure
    5.5    Key Industrial Trends
6    Market Snapshot
    6.1    Global
    6.2    Region
7    Opportunities and Challenges in the Market
8    Global Morquio Syndrome Treatment Market Analysis

    8.1    Key Industry Highlights
    8.2    Global Morquio Syndrome Treatment Historical Market (2018-2023) 
    8.3    Global Morquio Syndrome Treatment Market Forecast (2024-2032)
    8.4    Global Morquio Syndrome Treatment Market by Disease Type
        8.4.1    Morquio A
            8.4.1.1    Market Share
            8.4.1.2    Historical Trend (2018-2023)
            8.4.1.3    Forecast Trend (2024-2032)
        8.4.2    Morquio B
            8.4.2.1    Market Share
            8.4.2.2    Historical Trend (2018-2023)
            8.4.2.3    Forecast Trend (2024-2032)
    8.5    Global Morquio Syndrome Treatment Market by Treatment
        8.5.1    Enzyme Replacement Therapy
            8.5.1.1    Market Share
            8.5.1.2    Historical Trend (2018-2023)
            8.5.1.3    Forecast Trend (2024-2032)
        8.5.2    Others
    8.6    Global Morquio Syndrome Treatment Market by Distribution Channels
        8.6.1    Hospital Pharmacies
            8.6.1.1    Market Share
            8.6.1.2    Historical Trend (2018-2023)
            8.6.1.3    Forecast Trend (2024-2032)
        8.6.2    Retail Pharmacies
            8.6.2.1    Market Share
            8.6.2.2    Historical Trend (2018-2023)
            8.6.2.3    Forecast Trend (2024-2032)
        8.6.3    Online
            8.6.3.1    Market Share
            8.6.3.2    Historical Trend (2018-2023)
            8.6.3.3    Forecast Trend (2024-2032)
    8.7    Global Morquio Syndrome Treatment Market by Region
        8.7.1    North America
            8.7.1.1    Market Share
            8.7.1.2    Historical Trend (2018-2023) 
            8.7.1.3    Forecast Trend (2024-2032)
        8.7.2    Europe
            8.7.2.1    Market Share
            8.7.2.2    Historical Trend (2018-2023) 
            8.7.2.3    Forecast Trend (2024-2032)
        8.7.3    Asia Pacific
            8.7.3.1    Market Share
            8.7.3.2    Historical Trend (2018-2023) 
            8.7.3.3    Forecast Trend (2024-2032)
        8.7.4    Latin America
            8.7.4.1    Market Share
            8.7.4.2    Historical Trend (2018-2023) 
            8.7.4.3    Forecast Trend (2024-2032)
        8.7.5    Middle East and Africa
            8.7.5.1    Market Share
            8.7.5.2    Historical Trend (2018-2023) 
            8.7.5.3    Forecast Trend (2024-2032)
9    North America Market Analysis
    9.1    United States of America 
        9.1.1    Market Share
        9.1.2    Historical Trend (2018-2023) 
        9.1.3    Forecast Trend (2024-2032)
    9.2    Canada
        9.2.1    Market Share
        9.2.2    Historical Trend (2018-2023) 
        9.2.3    Forecast Trend (2024-2032)
10    Europe Market Analysis
    10.1    United Kingdom
        10.1.1    Market Share
        10.1.2    Historical Trend (2018-2023) 
        10.1.3    Forecast Trend (2024-2032)
    10.2    Germany
        10.2.1    Market Share
        10.2.2    Historical Trend (2018-2023) 
        10.2.3    Forecast Trend (2024-2032)
    10.3    France
        10.3.1    Market Share
        10.3.2    Historical Trend (2018-2023) 
        10.3.3    Forecast Trend (2024-2032)
    10.4    Italy
        10.4.1    Market Share
        10.4.2    Historical Trend (2018-2023) 
        10.4.3    Forecast Trend (2024-2032)
    10.5    Others
11    Asia Pacific Market Analysis
    11.1    China
        11.1.1    Market Share
        11.1.2    Historical Trend (2018-2023) 
        11.1.3    Forecast Trend (2024-2032)
    11.2    Japan
        11.2.1    Market Share
        11.2.2    Historical Trend (2018-2023) 
        11.2.3    Forecast Trend (2024-2032)
    11.3    India
        11.3.1    Market Share
        11.3.2    Historical Trend (2018-2023) 
        11.3.3    Forecast Trend (2024-2032)
    11.4    ASEAN
        11.4.1    Market Share
        11.4.2    Historical Trend (2018-2023) 
        11.4.3    Forecast Trend (2024-2032)
    11.5    Australia
        11.5.1    Market Share
        11.5.2    Historical Trend (2018-2023) 
        11.5.3    Forecast Trend (2024-2032)
    11.6    Others
12    Latin America Market Analysis
    12.1    Brazil
        12.1.1    Market Share
        12.1.2    Historical Trend (2018-2023) 
        12.1.3    Forecast Trend (2024-2032)
    12.2    Argentina
        12.2.1    Market Share
        12.2.2    Historical Trend (2018-2023) 
        12.2.3    Forecast Trend (2024-2032)
    12.3    Mexico
        12.3.1    Market Share
        12.3.2    Historical Trend (2018-2023) 
        12.3.3    Forecast Trend (2024-2032)
    12.4    Others
13    Middle East and Africa Market Analysis
    13.1    Saudi Arabia
        13.1.1    Market Share
        13.1.2    Historical Trend (2018-2023) 
        13.1.3    Forecast Trend (2024-2032)
    13.2    United Arab Emirates
        13.2.1    Market Share
        13.2.2    Historical Trend (2018-2023) 
        13.2.3    Forecast Trend (2024-2032)
    13.3    Nigeria
        13.3.1    Market Share
        13.3.2    Historical Trend (2018-2023) 
        13.3.3    Forecast Trend (2024-2032)
    13.4    South Africa
        13.4.1    Market Share
        13.4.2    Historical Trend (2018-2023) 
        13.4.3    Forecast Trend (2024-2032)
    13.5    Others
14    Market Dynamics
    14.1    SWOT Analysis
        14.1.1    Strengths
        14.1.2    Weaknesses
        14.1.3    Opportunities
        14.1.4    Threats
    14.2    Porter’s Five Forces Analysis
        14.2.1    Supplier’s Power
        14.2.2    Buyer’s Power
        14.2.3    Threat of New Entrants
        14.2.4    Degree of Rivalry
        14.2.5    Threat of Substitutes
    14.3    Key Indicators for Demand
    14.4    Key Indicators for Price
15    Competitive Landscape
    15.1    Market Structure
    15.2    Company Profiles
        15.2.1    BioMarin Pharmaceutical Inc.
            15.2.1.1    Company Overview
            15.2.1.2    Product Portfolio
            15.2.1.3    Demographic Reach and Achievements
            15.2.1.4    Certifications
        15.2.2    JCR Pharmaceuticals Co., Ltd.
            15.2.2.1    Company Overview
            15.2.2.2    Product Portfolio
            15.2.2.3    Demographic Reach and Achievements
            15.2.2.4    Certifications
        15.2.3    Sanofi
            15.2.3.1    Company Overview
            15.2.3.2    Product Portfolio
            15.2.3.3    Demographic Reach and Achievements
            15.2.3.4    Certifications
        15.2.4    Sangamo Therapeutics
            15.2.4.1    Company Overview
            15.2.4.2    Product Portfolio
            15.2.4.3    Demographic Reach and Achievements
            15.2.4.4    Certifications
        15.2.5    Alexion Pharmaceuticals Inc.
            15.2.5.1    Company Overview
            15.2.5.2    Product Portfolio
            15.2.5.3    Demographic Reach and Achievements
            15.2.5.4    Certifications
        15.2.6    Others
16    Key Trends and Developments in the Market


List of Key Figures and Tables

1.    Global Morquio Syndrome Treatment Market: Key Industry Highlights, 2018 and 2032
2.    Global Morquio Syndrome Treatment Historical Market: Breakup by Disease Type (USD Million), 2018-2023
3.    Global Morquio Syndrome Treatment Market Forecast: Breakup by Disease Type (USD Million), 2024-2032
4.    Global Morquio Syndrome Treatment Historical Market: Breakup by Treatment (USD Million), 2018-2023
5.    Global Morquio Syndrome Treatment Market Forecast: Breakup by Treatment (USD Million), 2024-2032
6.    Global Morquio Syndrome Treatment Historical Market: Breakup by Distribution Channels (USD Million), 2018-2023
7.    Global Morquio Syndrome Treatment Market Forecast: Breakup by Distribution Channels (USD Million), 2024-2032
8.    Global Morquio Syndrome Treatment Historical Market: Breakup by Region (USD Million), 2018-2023
9.    Global Morquio Syndrome Treatment Market Forecast: Breakup by Region (USD Million), 2024-2032
10.    North America Morquio Syndrome Treatment Historical Market: Breakup by Country (USD Million), 2018-2023
11.    North America Morquio Syndrome Treatment Market Forecast: Breakup by Country (USD Million), 2024-2032
12.    Europe Morquio Syndrome Treatment Historical Market: Breakup by Country (USD Million), 2018-2023
13.    Europe Morquio Syndrome Treatment Market Forecast: Breakup by Country (USD Million), 2024-2032
14.    Asia Pacific Morquio Syndrome Treatment Historical Market: Breakup by Country (USD Million), 2018-2023
15.    Asia Pacific Morquio Syndrome Treatment Market Forecast: Breakup by Country (USD Million), 2024-2032
16.    Latin America Morquio Syndrome Treatment Historical Market: Breakup by Country (USD Million), 2018-2023
17.    Latin America Morquio Syndrome Treatment Market Forecast: Breakup by Country (USD Million), 2024-2032
18.    Middle East and Africa Morquio Syndrome Treatment Historical Market: Breakup by Country (USD Million), 2018-2023
19.    Middle East and Africa Morquio Syndrome Treatment Market Forecast: Breakup by Country (USD Million), 2024-2032
20.    Global Morquio Syndrome Treatment Market Structure.

Key Questions Answered in the Report

The market is expected to grow at a CAGR of 5.70% during the period 2024-2032.

The market is driven by the growing demand for specialized medications and increasing collaborative efforts by the market players to introduce innovative treatment methods.

The increasing number of innovative and approved treatment methods and the rising number of government initiatives to support research and development in the healthcare sector is expected to deliver new growth opportunities to the market.

The regional markets for the global market include North America, Europe, the Asia Pacific, Latin America, the Middle East and Africa.

The disease types in morquio syndrome treatment include morquio A and morquio B.

The various treatments for morquio syndrome treatment include enzyme replacement therapy and others.

The market for morquio syndrome treatment uses various distribution channels including hospital pharmacies, retail pharmacies, and online.

The key players in the market include BioMarin Pharmaceutical Inc., JCR Pharmaceuticals Co., Ltd., Sanofi, Sangamo Therapeutics, and Alexion Pharmaceuticals Inc., among others.

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